Stem Cell Therapy in Lysosomal Storage Diseases

Offers multidisciplinary input – from the clinic and the laboratory – into the management of LSD using cellular therapies, summarizing the recent and enormous changes in this field

Examines the current roles of treatments, including newer ones, and how they may be used in combination to treat these rare diseases

Provides state of the art treatment that can be implemented in daily practice and looks at possible long and short term future developments